Chapter
Targeting Spinal and Bulbar Muscular Atrophy
From Share your story with the Oxford-Harrington Rare Disease Centre by öxford-Harrington RARE DISEASE CENTRE
Concepts
- Mutant Receptors
"Professor Carlo Rinaldi, 2024 Oxford-Harrington Rare Disease Scholar, is developing a therapy to target mutant androgen receptors in spinal and bulbar muscular atrophy."